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Dernières publications
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Valentina Taglietti, Kaouthar Kefi, Lea Rivera, Oriane Bergiers, Nastasia Cardone, et al.. Thyroid-stimulating hormone receptor signaling restores skeletal muscle stem cell regeneration in rats with muscular dystrophy. Science Translational Medicine, 2023, 15 (685), ⟨10.1126/scitranslmed.add5275⟩. ⟨hal-04150315⟩
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A. Morin, Amalia Stantzou, Olga N. Petrova, John C.W. Hildyard, T. Tensorer, et al.. Dystrophin myonuclear domain restoration governs treatment efficacy in dystrophic muscle. Proceedings of the National Academy of Sciences of the United States of America, 2023, 120 (2), ⟨10.1073/pnas.2206324120⟩. ⟨hal-04122777⟩
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Chiffres clés
55
Publications with fulltext
Open Access
76 %
Mots clés
Multi exon skipping
Long noncoding RNA
Ex-vivo
Molecular Sequence Data
Multiresolution modeling
Inbred C57BL
LKB1
Dystrophie myotonique de type 1 DM1
Becker muscular dystrophy
Becker Muscular Dystrophy
Connexins
Autophagy
Modificateurs de gènes
Becker BMD muscular dystrophy
Male
Cultured
DHPR α1S
Gene expression
MES
Skeletal muscle
DMO
Dilated Cardiomyopathy
Dynamin 2
Humans
Drp1
Jonction neuromusculaire JNM
Antisense oligonucleotides
Duchenne DMD dystrophy
Mitochondrial fission
Base Sequence
Inhibitors
Calcium Channels
Cachexia
LncARN
Immunoglobulin Fc Fragments/pharmacology
Metabolism
CaVβ1
Génomique
Cardiomyopathie
Energy Metabolism/drug effects
Cardiomyopathy
Calcium
CTNNB1
Dystrophin-EGFP
Cell Line
Animals
Animal/physiopathology
L-Type
Diseases
Clinical trials
Delivery
Muscle
Becker muscular dystrophy BMD
Heart Failure
Hear
Duchenne muscular dystrophy DMD
Dystrophie musculaire de Becker
Dystrophie Musculaire de Becker BMD
Isoforms
CD38
Epigenetics
Genomic
Centronuclear myopathy
Isoformes
Activin Receptors
DMD
Dystrophie Musculaire de Duchenne DMD
CaV subunits
Duchenne muscular dystrophy
Multi resolution modeling
Adult muscle stem cells
Human Umbilical Vein Endothelial Cells
Gene Expression Regulation/drug effects
Molecular docking
Invivo
Inbred mdx
Mice
Morphogenesis
MiARN
Cell homeostasis
Gene modifiers
CaVβs
Long QT
Mdx mouse
Liver
Becker muscular dystrophy BMD Duchenne muscular dystrophy DMD miRNA nNOS
Homeostasis
BMD
Cell Biology
Cells
Dystrophy
Dystrophine
Exon skipping
Muscle Biology
LncRNA
Knockout
Dystrophin
Allele‐specific silencing therapy
Dystrophin central domain
Hepatocellular carcinoma